genetische therapie voor ultra-zeldzaam
11-03-2026 Burumazaal, Onderwijsgebouw LUMC, Leiden
RARE-NL @LUMC – Antisense oligonucleotides for n-of-few: on the way to the clinic 13:30h - 17:30h
This RARE-NL meeting on 11 March at LUMC focuses on the development and implementation of antisense oligonucleotides for n-of-few and n-of-1 indications. The meeting brings together researchers, clinicians and experts in access pathways to explore how ASOs can be translated into clinical practice. The emphasis is on shared challenges and solutions that require collaboration beyond individual UMCs.

registreer hier Registration Form - March 11, 2026